Europe — EMA
Onpattro (Patisiran)
Patisiran, the active ingredient in Onpattro, is a RNA RNA ? presented as a for use. It treats hereditary transthyretin-mediated amyloidosis in adults.
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What is Patisiran?
Patisiran, the active ingredient in Onpattro, is a RNA RNA ? presented as a for use. It treats hereditary transthyretin-mediated amyloidosis in adults.
GNH USA supplies Onpattro as a licensed, GDP‑compliant international pharmaceutical supplier serving hospitals worldwide.
What is Patisiran used for?
Onpattro is used in the management of hereditary transthyretin‑mediated amyloidosis, a rare genetic disorder.
- Hereditary transthyretin‑mediated amyloidosis: Improves the outcome by reducing the toxic protein deposits in the nerves and muscle tissues. - ");" "
Product details
Drug
Patisiran
Route
Intravenous Use
Manufacturer
Alnylam Netherlands B.V.
Origin
EU


